{"id":17254,"date":"2023-12-15T19:57:13","date_gmt":"2023-12-15T18:57:13","guid":{"rendered":"https:\/\/www.hematostat.net\/?p=17254"},"modified":"2024-01-02T20:00:07","modified_gmt":"2024-01-02T19:00:07","slug":"vertex-recoit-lavis-positif-du-chmp-pour-la-premiere-therapie-genique-crispr-cas9-casgevy-exagamglogene-autotemcel-dans-le-traitement-de-la-drepanocytose-severe-et-de-la-beta-thalassemie-de","status":"publish","type":"post","link":"https:\/\/www.hematostat.net\/en\/vertex-recoit-lavis-positif-du-chmp-pour-la-premiere-therapie-genique-crispr-cas9-casgevy-exagamglogene-autotemcel-dans-le-traitement-de-la-drepanocytose-severe-et-de-la-beta-thalassemie-de\/","title":{"rendered":"Vertex re\u00e7oit l&#8217;avis positif du CHMP pour la premi\u00e8re th\u00e9rapie g\u00e9nique CRISPR\/Cas9, CASGEVY\u00ae (exagamglog\u00e8ne autotemcel) dans le traitement de la dr\u00e9panocytose s\u00e9v\u00e8re et de la b\u00eata-thalass\u00e9mie d\u00e9pendante des transfusions."},"content":{"rendered":"<p class=\"p1\"><span class=\"Apple-converted-space\">\u00a0<\/span><\/p>\n<ul>\n<li class=\"p2\">Sous r\u00e9serve d&#8217;approbation par la Commission europ\u00e9enne, certains patients \u00e2g\u00e9s de 12 ans et plus atteints de dr\u00e9panocytose s\u00e9v\u00e8re ou de b\u00eata-thalass\u00e9mie d\u00e9pendante des transfusions, pour lesquels une transplantation de cellules souches h\u00e9matopo\u00ef\u00e9tiques est appropri\u00e9e et pour lesquels un donneur apparent\u00e9 compatible avec l&#8217;antig\u00e8ne leucocytaire humain n&#8217;est pas disponible, seraient \u00e9ligibles pour le traitement.<\/li>\n<li class=\"p2\"><span class=\"Apple-converted-space\"> La d\u00e9cision d&#8217;approbation de la Commission europ\u00e9enne est attendue pour le premier trimestre 2024.<\/span><\/li>\n<\/ul>\n<p class=\"p2\" style=\"text-align: right;\"><i>D&#8217;apr\u00e8s un communiqu\u00e9 de presse de Vertex le 15 d\u00e9cembre 2023.<\/i><\/p>","protected":false},"excerpt":{"rendered":"<p>\u00a0 Sous r\u00e9serve d&#8217;approbation par la Commission europ\u00e9enne, certains patients \u00e2g\u00e9s de 12 ans et plus atteints de dr\u00e9panocytose s\u00e9v\u00e8re ou de b\u00eata-thalass\u00e9mie d\u00e9pendante des transfusions, pour lesquels une transplantation [&hellip;]<\/p>","protected":false},"author":1,"featured_media":0,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"_monsterinsights_skip_tracking":false,"_monsterinsights_sitenote_active":false,"_monsterinsights_sitenote_note":"","_monsterinsights_sitenote_category":0,"_uf_show_specific_survey":0,"_uf_disable_surveys":false,"footnotes":""},"categories":[21],"tags":[],"ppma_author":[441],"class_list":["post-17254","post","type-post","status-publish","format-standard","hentry","category-communique-de-presse","author-admin6779"],"aioseo_notices":[],"authors":[{"term_id":441,"user_id":1,"is_guest":0,"slug":"admin6779","display_name":"HematoStat.net","avatar_url":"https:\/\/secure.gravatar.com\/avatar\/4f64711e55fa3c9401676697c4783cec15305a6f940a0f120048b6141a611347?s=96&d=mm&r=g","first_name":"HematoStat.net","last_name":"","user_url":"http:\/\/www.hematostat.net","description":""}],"_links":{"self":[{"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/posts\/17254","targetHints":{"allow":["GET"]}}],"collection":[{"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/types\/post"}],"author":[{"embeddable":true,"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/users\/1"}],"replies":[{"embeddable":true,"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/comments?post=17254"}],"version-history":[{"count":1,"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/posts\/17254\/revisions"}],"predecessor-version":[{"id":17256,"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/posts\/17254\/revisions\/17256"}],"wp:attachment":[{"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/media?parent=17254"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/categories?post=17254"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/tags?post=17254"},{"taxonomy":"author","embeddable":true,"href":"https:\/\/www.hematostat.net\/en\/wp-json\/wp\/v2\/ppma_author?post=17254"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}